Metabolic stress and early cell death in photoreceptor precursor cells following retinal transplantation
AAV2.7m8 transduction of stage 2 human retinal organoids induces highly variable responses in innate and inflammatory gene expression and cytokine secretion
iPS cell modeling of Best disease: insights into the pathophysiology of an inherited macular degeneration
Genome-Wide CRISPR Screening Identifies Cellular Factors Controlling Nonviral Genome Editing Efficiency
Robust generation of photoreceptor-dominant retinal organoids from porcine induced pluripotent stem cells
Evaluation of subretinally delivered Cas9 ribonucleoproteins in murine and porcine animal models highlights key considerations for therapeutic translation of genetic medicines
